Risdiplam
Evrysdi (risdiplam) is a small molecule pharmaceutical. Risdiplam was first approved as Evrysdi on 2020-08-07. It has been approved in Europe to treat spinal muscular atrophy. Evrysdi's patents are valid until 2035-05-11 (FDA).
Trade Name | Evrysdi |
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Common Name | Risdiplam |
Indication | spinal muscular atrophy |
Drug Class | Survival motor neurin SMN1 and SMN2 splicing modulators |