Eteplirsen
Exondys (eteplirsen) is an oligonucleotide pharmaceutical. Eteplirsen was first approved as Exondys on 2016-09-19. It is used to treat duchenne muscular dystrophy in the USA. Exondys 51's patents are valid until 2034-03-14 (FDA).
Trade Name | Exondys |
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Common Name | Eteplirsen |
Indication | duchenne muscular dystrophy |
Drug Class | Antisense oligonucleotides |
